Tag Archive for: Tissue

FDA adcomm sides with Vertex, CRISPR on safety testing for SCD gene therapy

The regulator’s advisory committee on Tuesday found Vertex Pharmaceuticals and CRISPR Therapeutics’ off-target analysis for its sickle cell disease candidate exa-cel to be sufficient.

Read more
/by

Bluebird bio’s blood disorder therapy effective – FDA staff

,

Bluebird bio’s blood disorder treatment demonstrates “clinically meaningful” benefit in patients, staff reviewers at the U.S. Food and Drug Administration said in briefing documents published on Tuesday.

Read more
/by